Development of an AAV-Based MicroRNA Gene Therapy to Treat Machado-Joseph Disease

Martier, Raygene; Sogorb-Gonzalez, Marina; Stricker-Shaver, Janice; Huebener-Schmid, Jeannette; Keskin, Sonay; Klima, Jiri; Toonen, Lodewijk J.; Juhas, Stefan; Juhasova, Jana; Ellederova, Zdenka; Motlik, Jan; Haas, Eva; van Deventer, Sander; Konstantinova, Pavlina; Huu Phuc Nguyen; Evers, Melvin M.

Development of an AAV-Based MicroRNA Gene Therapy to Treat Machado-Joseph Disease

Autor(en):

Martier, Raygene; Sogorb-Gonzalez, Marina; Stricker-Shaver, Janice; Huebener-Schmid, Jeannette; Keskin, Sonay; Klima, Jiri; Toonen, Lodewijk J.; Juhas, Stefan; Juhasova, Jana; Ellederova, Zdenka; Motlik, Jan; Haas, Eva; van Deventer, Sander; Konstantinova, Pavlina; Huu Phuc Nguyen; Evers, Melvin M.

Tübinger Autor(en):

Stricker-Shaver, Janice
Hübener-Schmid, Jeannette
Haas, Eva

Erschienen in:

Molecular Therapy - Methods & Clinical Development (2019), Bd. 15, S. 343-358

Verlagsangabe:

Cell Press

Sprache:

Englisch

Referenz zum Volltext:

http://dx.doi.org/10.1016/j.omtm.2019.10.008

ISSN:

2329-0501