Single-guide RNA Cas9 and enhanced-deletion Cas9 rescue a recurrent USH2A-related splicing defect

De Angeli, Pietro; Spaag, Salome; Shliaga, Stefanida; Flores-Tufino, Arturo; Ritter, Malte; Nasri, Masoud; Stingl, Katarina; Kuehlewein, Laura; Wissinger, Bernd; Kohl, Susanne

dc.contributor.author	De Angeli, Pietro
dc.contributor.author	Spaag, Salome
dc.contributor.author	Shliaga, Stefanida
dc.contributor.author	Ritter, Malte
dc.contributor.author	Stingl, Katarina
dc.contributor.author	Wissinger, Bernd
dc.contributor.author	Kohl, Susanne
dc.contributor.author	Flores-Tufiño, Arturo
dc.contributor.author	Nasri, Masoud
dc.contributor.author	Kühlewein, Laura
dc.date.accessioned	2025-10-01T13:28:52Z
dc.date.available	2025-10-01T13:28:52Z
dc.date.issued	2025
dc.identifier.issn	2162-2531
dc.identifier.uri	http://hdl.handle.net/10900/170508
dc.language.iso	en	de_DE
dc.publisher	Cambridge : Cell Press	de_DE
dc.relation.uri	http://dx.doi.org/10.1016/j.omtn.2025.102523	de_DE
dc.subject.ddc	610	de_DE
dc.title	Single-guide RNA Cas9 and enhanced-deletion Cas9 rescue a recurrent USH2A-related splicing defect	de_DE
dc.type	Article	de_DE
utue.quellen.id	20250630000000_01005
utue.personen.roh	De Angeli, Pietro
utue.personen.roh	Spaag, Salome
utue.personen.roh	Shliaga, Stefanida
utue.personen.roh	Flores-Tufino, Arturo
utue.personen.roh	Ritter, Malte
utue.personen.roh	Nasri, Masoud
utue.personen.roh	Stingl, Katarina
utue.personen.roh	Kuehlewein, Laura
utue.personen.roh	Wissinger, Bernd
utue.personen.roh	Kohl, Susanne
dcterms.isPartOf.ZSTitelID	Molecular Therapy Nucleic Acids	de_DE
dcterms.isPartOf.ZS-Issue	2	de_DE
dcterms.isPartOf.ZS-Volume	36	de_DE
utue.fakultaet	04 Medizinische Fakultät	de_DE